A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.
Researchers described the case in a new study, saying he’s among the first to be successfully treated with a custom therapy that seeks to fix a tiny but critical error in his genetic code that kills half of affected infants. Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can someday help the millions left behind even as genetic medicine has advanced because their conditions are so rare.
“This is the first step towards the use
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